欧美精品在线第一页,久久av影院,午夜视频在线播放一三,久久91精品久久久久久秒播,成人一区三区,久久综合狠狠综合久久狠狠色综合,成人av一区二区亚洲精,欧美a级在线观看
         
        First gene therapy for blindness gets 850,000-USD price tag in U.S.
                         Source: Xinhua | 2018-01-04 07:41:46 | Editor: huaxia

        International Blindness Relief Organization Vision Care President Dr. Dong Hae Kim (L) performs an eye cataract surgery during a three-day free eye surgical camp activity at Muhimbili National Hospital in Dar es Salaam, Tanzania, Aug. 9, 2016. The activity is held in partnership with Muhimbili University of Health and Allied Sciences (MUHAS). More than 25 patients underwent eyes surgery within two days. (Xinhua/John Badi)

        WASHINGTON, Jan. 3 (Xinhua) -- Luxturna, the first gene therapy approved in the United States for a rare, inherited form of blindness, will cost 850,000 U.S. dollars per patient, its maker announced on Wednesday.

        "The Wholesale Acquisition Cost of one-time LUXTURNA is 425,000 dollars per eye," Monique da Silva, a spokeswoman for Sparks Therapeutics, told Xinhua in an email.

        "The price reflects the stakeholder considerations we have learned about these past months, including access concerns of patients, families, health care providers and treatment centers."

        While the price came in lower than the one-million-dollar estimate by U.S. analysts, it's still among the most expensive treatments in the world.

        Spark Therapeutics said it will offer rebates to health insurers if the treatment does not work.

        The company said it has reached agreement in principle with Boston-based insurer Harvard Pilgrim to offer the outcomes-based rebate arrangement and is also in active discussions with other commercial insurers regarding this offering.

        Spark Therapeutics also said it's addressing budgetary concerns by working towards multiple solutions to allow installment payments over multiple years.

        An international research team led by Chinese scientists has found a new gene that can cause congenital blindness. (Xinhua file photo by Lin Hong)

        Luxturna was approved last month by U.S. Food and Drug Administration (FDA) to treat children and adult patients with confirmed biallelic RPE65 mutation-associated retinal dystrophy that leads to vision loss and may cause complete blindness in certain patients.

        It works by delivering a normal copy of the RPE65 gene directly to retinal cells, leading these cells to produce the normal protein that converts light to an electrical signal in the retina to restore patient's vision loss.

        Prior to this approval, the FDA greenlighted two other gene therapies that re-engineer people's own immune cells to treat blood cancers.

        Both came with hefty price tags. Yescarta, a drug that treats certain types of large B-cell lymphoma, has a price tag of 373,000 dollars. Kymriah, a leukemia therapy, is similarly expensive at 475,000 dollars.

        Back to Top Close
        Xinhuanet

        First gene therapy for blindness gets 850,000-USD price tag in U.S.

        Source: Xinhua 2018-01-04 07:41:46

        International Blindness Relief Organization Vision Care President Dr. Dong Hae Kim (L) performs an eye cataract surgery during a three-day free eye surgical camp activity at Muhimbili National Hospital in Dar es Salaam, Tanzania, Aug. 9, 2016. The activity is held in partnership with Muhimbili University of Health and Allied Sciences (MUHAS). More than 25 patients underwent eyes surgery within two days. (Xinhua/John Badi)

        WASHINGTON, Jan. 3 (Xinhua) -- Luxturna, the first gene therapy approved in the United States for a rare, inherited form of blindness, will cost 850,000 U.S. dollars per patient, its maker announced on Wednesday.

        "The Wholesale Acquisition Cost of one-time LUXTURNA is 425,000 dollars per eye," Monique da Silva, a spokeswoman for Sparks Therapeutics, told Xinhua in an email.

        "The price reflects the stakeholder considerations we have learned about these past months, including access concerns of patients, families, health care providers and treatment centers."

        While the price came in lower than the one-million-dollar estimate by U.S. analysts, it's still among the most expensive treatments in the world.

        Spark Therapeutics said it will offer rebates to health insurers if the treatment does not work.

        The company said it has reached agreement in principle with Boston-based insurer Harvard Pilgrim to offer the outcomes-based rebate arrangement and is also in active discussions with other commercial insurers regarding this offering.

        Spark Therapeutics also said it's addressing budgetary concerns by working towards multiple solutions to allow installment payments over multiple years.

        An international research team led by Chinese scientists has found a new gene that can cause congenital blindness. (Xinhua file photo by Lin Hong)

        Luxturna was approved last month by U.S. Food and Drug Administration (FDA) to treat children and adult patients with confirmed biallelic RPE65 mutation-associated retinal dystrophy that leads to vision loss and may cause complete blindness in certain patients.

        It works by delivering a normal copy of the RPE65 gene directly to retinal cells, leading these cells to produce the normal protein that converts light to an electrical signal in the retina to restore patient's vision loss.

        Prior to this approval, the FDA greenlighted two other gene therapies that re-engineer people's own immune cells to treat blood cancers.

        Both came with hefty price tags. Yescarta, a drug that treats certain types of large B-cell lymphoma, has a price tag of 373,000 dollars. Kymriah, a leukemia therapy, is similarly expensive at 475,000 dollars.

        010020070750000000000000011100001368704011
        主站蜘蛛池模板: 91看片免费| 国产69精品久久99不卡解锁版| 欧美一区二区三区不卡视频| 国产精品自产拍在线观看蜜| 中文字幕国内精品| 欧美髙清性xxxxhdvid| 日韩午夜毛片| 国产色婷婷精品综合在线播放| 精品一区二区三区影院| 免费看片一区二区三区| 久久午夜精品福利一区二区 | 精品国产伦一区二区三区免费| 久久黄色精品视频| 国产乱一乱二乱三| 中文字幕制服狠久久日韩二区| 日本一二区视频| 国产精品不卡在线| 夜夜嗨av一区二区三区中文字幕| 夜夜躁日日躁狠狠久久av| 国产一区二区四区| 久久人人爽爽| 日韩av中文字幕在线免费观看| 香蕉av一区二区| 欧美日韩国产一二| 欧美xxxxxhd| 日韩国产精品一区二区| 日韩精品在线一区二区三区| 国产有码aaaae毛片视频| 清纯唯美经典一区二区| 国产一区二区在线91| 国久久久久久| 亚洲va国产| 高清人人天天夜夜曰狠狠狠狠| 欧美精品一区二区三区四区在线| 国产精品18久久久久白浆| 色综合久久综合| 91精品色| 国产精品久久久久久久久久久杏吧 | 91精品www| 精品在线观看一区二区| 狠狠色噜噜狠狠狠狠米奇777| 草逼视频网站| 亚洲第一天堂无码专区| 国产精品自产拍在线观看蜜| 日韩午夜三级| 日韩精品一区二区av| 久久精品一| 国产精品电影一区二区三区| 亚洲精品一区中文字幕| 国产精品电影一区二区三区| 性国产日韩欧美一区二区在线| 国产精品一区不卡| 国产一区二区国产| 91一区在线| 欧美在线视频三区| 国产一区在线免费| 国产亚洲精品久久网站| 国产精品电影免费观看| 欧美一区二区在线不卡| 久久99精品一区二区三区| 四季av中文字幕一区| 欧美一区二区三区白人| 日韩av片无码一区二区不卡电影| 手机看片国产一区| 一本色道久久综合亚洲精品图片| 欧美精品久久一区二区| 狠狠色噜狠狠狠狠| 91国内精品白嫩初高生| 在线精品视频一区| 午夜毛片在线观看| 国产精品高潮呻| 国产69精品久久久久男男系列| 国产国产精品久久久久| 国产乱码精品一区二区三区介绍| 午夜影院伦理片| 国产69精品久久久久孕妇不能看| 久久久一区二区精品| 精品国产一区在线| 国产一级不卡视频| 亚洲国产偷| 精品欧美一区二区精品久久小说| 综合久久色| 中文字幕在线一区二区三区| 性国产videofree极品| 国产在线一卡| 欧美乱妇高清无乱码一级特黄| 久久久中精品2020中文| 性少妇freesexvideos高清bbw| 国产一区免费播放| 激情久久综合网| 久久久久亚洲| 亚洲**毛茸茸| 日韩av中文字幕第一页| 日韩一区免费| 日本三级香港三级网站| 国产精品免费一视频区二区三区 | 亚洲视频h| 国产目拍亚洲精品区一区| 毛片大全免费观看| 亚洲精品乱码久久久久久高潮| 日韩中文字幕亚洲欧美| 亚洲欧美日韩在线看| 狠狠躁狠狠躁视频专区| 午夜在线看片| 国产日韩欧美亚洲| 国产伦理久久精品久久久久| 狠狠躁天天躁又黄又爽| 欧美一区二区免费视频| 亚洲美女在线一区| 日本xxxxxxxxx68护士| 少妇厨房与子伦在线观看| 国产一区二区影院| 国产午夜精品一区二区三区最新电影 | 中文字幕日韩有码| 国产乱淫精品一区二区三区毛片| 中文字幕国内精品| 国产欧美日韩另类| 国产在线拍偷自揄拍视频 | 日本黄页在线观看| 少妇高潮一区二区三区99小说| 欧美69精品久久久久久不卡| 久久综合伊人77777麻豆| 国产精品一区二区久久乐夜夜嗨| 一区二区在线不卡| 欧美日韩一区二区高清| 欧美极品少妇xx高潮| 国产日韩一区二区在线| 爽妇色啪网| 久久综合国产精品| 国产伦理精品一区二区三区观看体验| 国产精品欧美久久久久一区二区| 午夜影院激情| 欧美日韩一级在线观看| 欧美xxxxhdvideos| 国产美女三级无套内谢| 亚洲精品久久久中文| 精品国产一二区| 精品99在线视频| 欧美一区二区三区四区五区六区| 欧美精品日韩精品| 国产1区在线观看| 国产高清在线一区| 国产视频一区二区在线播放| 欧美精品亚洲一区| 97精品国产aⅴ7777| 一级午夜电影| 久久96国产精品久久99软件| 农村妇女精品一区二区| 国产精品一区在线观看| 国产高清一区二区在线观看| 色综合欧美亚洲国产| 中文字幕在线播放一区| 国产精品久久久久久久久久久久久久久久| 高清国产一区二区三区| 日韩精品一区中文字幕| 欧美精品在线不卡| 午夜激情在线播放| 一区二区三区四区视频在线| 狠狠躁日日躁狂躁夜夜躁| 欧美精品第1页| 理论片午午伦夜理片在线播放 | 日韩午夜毛片| 国内自拍偷拍一区| 久久青草欧美一区二区三区| 99久久国产综合| 国产欧美日韩一区二区三区四区| 少妇又紧又色又爽又刺激视频网站| 亚洲影院久久| 亚洲神马久久| 精品一区电影国产| 午夜黄色网址| 久久久久久久亚洲视频| 欧美视频1区| 91麻豆精品国产自产欧美一级在线观看| 国产高清一区在线观看| 正在播放国产一区二区| 国产精品对白刺激在线观看| 男女午夜爽爽| 国产69精品久久久久app下载 | 国产视频二区在线观看| 一二三区欧美| 538国产精品| 日韩av一区二区在线播放| 中文丰满岳乱妇在线观看| 性国产日韩欧美一区二区在线| 中文字幕制服狠久久日韩二区| 国产伦精品一区二| 国产精品亚洲二区| 国产性猛交| 午夜国产一区二区三区四区| 国内久久精品视频| 亚洲欧美国产精品一区二区| 国产视频精品一区二区三区| 午夜片在线| 国产精品久久久久久久久久久不卡| 日韩av视屏在线观看| 亚洲乱玛2021| 欧洲激情一区二区| 亚洲欧美日韩三区| 欧美在线播放一区| 午夜黄色大片| 狠狠躁夜夜| 国产精品视频99| 最新日韩一区| 香港日本韩国三级少妇在线观看| 亚洲精品少妇一区二区| 岛国黄色av| 国产午夜三级一区二区三| 国产天堂一区二区三区| 国产亚洲精品久久久久动| 久久国产精品波多野结衣| 在线精品国产一区二区三区 | 国产一区二区日韩| 欧美日韩国产综合另类| 久久99精品久久久久婷婷暖91 | 欧美精品日韩| 久久综合二区| 国产午夜精品一区二区理论影院| 日韩美一区二区三区| 欧美激情精品久久久久久免费| 夜夜爽av福利精品导航| 久久99国产精品久久99果冻传媒新版本| 91看片app| 999偷拍精品视频| 欧美一区二区三区视频在线观看| 97久久精品人人做人人爽50路| 久久影视一区二区| 国产精品久久久久久久久久久新郎| 久久99精品国产| 欧美日韩精品在线播放| 欧美一级免费在线视频| 激情欧美日韩| 一区二区三区欧美视频| 久久久久国产精品视频| 欧美日韩国产影院| 久久久久国产精品一区二区三区| 国产一区www| 国产精品女人精品久久久天天| 国产精品二十区| 日韩av免费网站| 国产乱色国产精品播放视频| 护士xxxx18一19| 97人人澡人人爽91综合色| 亚洲精品乱码久久久久久高潮| 日韩久久精品一区二区| 亚洲精品国产91|